When pullulanase needs a little push: MyoAAV capsids enhance gene therapy for GSD IIIa

Sree Venigalla; Christina A. Pacak

doi:10.1016/j.omtm.2025.101648

When pullulanase needs a little push: MyoAAV capsids enhance gene therapy for GSD IIIa

Neurology

Research output: Contribution to journal › Comment/debate › peer-review

Original language	English (US)
Article number	101648
Journal	Molecular Therapy Methods and Clinical Development
Volume	33
Issue number	4
DOIs	https://doi.org/10.1016/j.omtm.2025.101648
State	Published - Dec 11 2025

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title = "When pullulanase needs a little push: MyoAAV capsids enhance gene therapy for GSD IIIa",

author = "Sree Venigalla and Pacak, \{Christina A.\}",

year = "2025",

month = dec,

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language = "English (US)",

volume = "33",

journal = "Molecular Therapy Methods and Clinical Development",

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T2 - MyoAAV capsids enhance gene therapy for GSD IIIa

AU - Venigalla, Sree

AU - Pacak, Christina A.

PY - 2025/12/11

Y1 - 2025/12/11

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DO - 10.1016/j.omtm.2025.101648

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JO - Molecular Therapy Methods and Clinical Development

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IS - 4

M1 - 101648

ER -

When pullulanase needs a little push: MyoAAV capsids enhance gene therapy for GSD IIIa

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