Twin Prime Editing Mediated Exon Skipping/Reinsertion for Restored Collagen VII Expression in Recessive Dystrophic Epidermolysis Bullosa

Benjamin J. Steinbeck, Xin D. Gao, Amber N. McElroy, Smriti Pandey, Jordan L. Doman, Megan J. Riddle, Lily Xia, Weili Chen, Cindy R. Eide, Andre H. Lengert, Sang Won Han, Bruce R. Blazar, Hans H. Wandall, Sally Dabelsteen, David R. Liu, Jakub Tolar, Mark J. Osborn

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Medicine and Dentistry

Biochemistry, Genetics and Molecular Biology