The End of the Beginning: The Journey to Molecular Therapies for Spinal Muscular Atrophy

Research output: Contribution to journalArticle

2 Scopus citations
Original languageEnglish (US)
Pages (from-to)1-2
Number of pages2
JournalPediatric Neurology
StatePublished - Jan 2020
Externally publishedYes


  • Genetic Therapy/economics
  • Humans
  • Muscular Atrophy, Spinal/economics

PubMed: MeSH publication types

  • Journal Article
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

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