Prolonged expression of a lysosomal enzyme in mouse liver after Sleeping Beauty transposon-mediated gene delivery: Implications for non-viral gene therapy of mucopolysaccharidoses

Elena L. Aronovich, Jason B. Bell, Lalitha R. Belur, Roland Gunther, Brenda Koniar, David C.C. Erickson, Patricia A. Schachern, Ilze Matise, R. Scott Mclvor, Chester B. Whitley, Perry B. Hackett

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Biochemistry, Genetics and Molecular Biology

Medicine and Dentistry