Onasemnogene abeparvovec preserves bulbar function in infants with presymptomatic spinal muscular atrophy: a post-hoc analysis of the SPR1NT trial

Richard D. Shell, Katlyn E. McGrattan, Rebecca Hurst-Davis, Sally Dunaway Young, Giovanni Baranello, Arseniy Lavrov, Eamonn O'Brien, Shiri Wallach, Nicole LaMarca, Sandra P. Reyna, Basil T. Darras

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Medicine and Dentistry

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