Long-term outcomes after allogeneic hematopoietic stem cell transplantation for metachromatic leukodystrophy: the largest single-institution cohort report

Keyphrases

• Allogeneic Hematopoietic Stem Cell Transplantation (allo-HSCT) 100%
• Metachromatic Leukodystrophy 100%
• Single Institution 100%
• Cohort Reports 100%
• Hematopoietic Stem Cell Transplantation 35%
• Nerve Conduction Velocity 15%
• Survivors 10%
• Brain MRI 10%
• Adaptive Functioning 10%
• Disease Progression 5%
• Natural History 5%
• Demyelinating Diseases 5%
• Single Center 5%
• Treatment Options 5%
• Quality of Life 5%
• Treatment-related 5%
• Neurologic 5%
• Life Expectancy 5%
• Activities of Daily Living 5%
• Sibling Pairs 5%
• Expressive Language 5%
• Symptom Status 5%
• Gross Motor 5%
• Late-onset 5%
• Neurologic Status 5%
• Late Infantile 5%
• Life Functioning 5%
• Neuropsychology 5%
• Data Survival 5%
• Global Decline 5%
• Clinical Scoring System 5%
• Language Functioning 5%
• Untreated Disease 5%
• Expressive Function 5%
• Novel Treatments 5%
• Gross Motor Function 5%
• Limited Treatment Options 5%
• Peripheral Nerve Conduction 5%

Medicine and Dentistry

• Allogeneic Hematopoietic Stem Cell Transplantation 100%
• Metachromatic Leukodystrophy 100%
• Hematopoietic Stem Cell Transplantation 35%
• Transplantation 25%
• Nerve Conduction Velocity 15%
• Magnetic Resonance Imaging of Brain 10%
• Disease 5%
• Magnetic Resonance Imaging 5%
• Quality of Life 5%
• Disease Exacerbation 5%
• Deterioration 5%
• Life Expectancy 5%
• Activities of Daily Living 5%
• Demyelinating Disorder 5%
• Scoring System 5%
• Peripheral Nerve 5%

Neuroscience

• Hematopoietic Cell 100%
• Metachromatic Leukodystrophy 100%
• Nerve Conduction 15%
• Magnetic Resonance Imaging of Brain 10%
• Magnetic Resonance Imaging 5%
• Peripheral Nerve 5%
• Neuropsychology 5%
• Demyelinating Disorder 5%