Hematopoietic stem-cell gene therapy for cerebral adrenoleukodystrophy

Florian Eichler, Christine Duncan, Patricia L. Musolino, Paul J. Orchard, Satiro De Oliveira, Adrian J. Thrasher, Myriam Armant, Colleen Dansereau, Troy C. Lund, Weston P. Miller, Gerald V. Raymond, Raman Sankar, Ami J. Shah, Caroline Sevin, H. Bobby Gaspar, Paul Gissen, Hernan Amartino, Drago Bratkovic, Nicholas J.C. Smith, Asif M. PakerEsther Shamir, Tara O’Meara, David Davidson, Patrick Aubourg, David A. Williams

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Medicine and Dentistry

Biochemistry, Genetics and Molecular Biology