Goal attainment in PMM2-CDG: A new approach measuring meaningful clinical outcomes
- Sanne Verberkmoes
- , Gina L. Mazza
- , Andrew C. Edmondson
- , Fernando Scaglia
- , Seishu Horikoshi
- , Bryce Kuschel
- , Mirian C.H. Janssen
- , Jehan Mousa
- , Austin Larson
- , Rameen Shah
- , Georgia McDonald
- , Kyriaki Sarafoglou
- , Gerard Berry
- , Tamas Kozicz
- , Christina Lam
- , Eva Morava
Research output: Contribution to journal › Article › peer-review
3
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