Gene therapy for genetic disease

J. A. Barranger, A. B. Bahnson, M. T. Nimgaonkar, E. D. Ball, Paul D Robbins, S. S. Boggs, T. Ohashi

Research output: Contribution to journalArticlepeer-review

5 Scopus citations


Gene therapy is a modality being studied for many diseases. Although most of the clinical applications are being considered for malignant disease, the origins of gene therapy lie in the inherited disease of metabolism. Gaucher disease serves as a prototype for the study of gene therapy for genetic disorders.

Original languageEnglish (US)
Pages (from-to)5-9
Number of pages5
JournalInternational Pediatrics
Issue number1
StatePublished - Jan 1 1995
Externally publishedYes

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