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Fabry disease, an under-recognized multisystemic disorder: Expert recommendations for diagnosis, management, and enzyme replacement therapy

  • Robert J. Desnick
  • , Roscoe Brady
  • , John Barranger
  • , Allan J. Collins
  • , Dominique P. Germain
  • , Martin Goldman
  • , Gregory Grabowski
  • , Seymour Packman
  • , William R. Wilcox

Research output: Contribution to journalReview articlepeer-review

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Pharmacology, Toxicology and Pharmaceutical Science

Medicine and Dentistry