Characterization of an immunodeficient mouse model of mucopolysaccharidosis type I suitable for preclinical testing of human stem cell and gene therapy

Mayra F. Garcia-Rivera, Leah E. Colvin-Wanshura, Matthew S. Nelson, Zhenhong Nan, Shaukat A. Khan, Tyson B. Rogers, Indrani Maitra, Walter C. Low, Pankaj Gupta

Research output: Contribution to journal › Article › peer-review

31 Scopus citations

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Keyphrases

Immunology and Microbiology

Biochemistry, Genetics and Molecular Biology

Neuroscience

Pharmacology, Toxicology and Pharmaceutical Science