Challenges in vector and trial design using retroviral vectors for long-term gene correction in hematopoietic stem cell gene therapy

Jacqueline Corrigan-Curay, Odile Cohen-Haguenauer, Marina O'Reilly, Susan R. Ross, Hung Fan, Naomi Rosenberg, Nikunj V Somia, Nancy King, Theodore Friedmann, Cynthia Dunbar, Alessandro Aiuti, Luigi Naldini, Christopher Baum, Christof Von Kalle, Hans Peter Kiem, Eugenio Montini, Frederic Bushman, Brian P. Sorrentino, Manuel Carrondo, Harry MalechGösta Gahrton, Robyn Shapiro, Linda Wolff, Eugene Rosenthal, Robert Jambou, John Zaia, Donald B. Kohn

Research output: Contribution to journalArticlepeer-review

42 Scopus citations
Original languageEnglish (US)
Pages (from-to)1084-1094
Number of pages11
JournalMolecular Therapy
Volume20
Issue number6
DOIs
StatePublished - Jun 2012

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