Bone marrow transplantation for globoid cell leukodystrophy, adrenoleukodystrophy, metachromatic leukodystrophy, and Hurler syndrome

William Krivit, Patrick Aubourg, Elsa Shapiro, Charles Peters

Research output: Contribution to journalArticlepeer-review

118 Scopus citations

Abstract

Bone marrow transplantation protocols for inherited metabolic storage diseases are unique for each disorder treated. Differences depend also upon how old the patient was when onset occurred and rate of progression of disease. Treatment is directed to prevent or ameliorate the inexorable neurological deterioration that is the major pathophysiological event in all of these inherited metabolic storage diseases.

Original languageEnglish (US)
Pages (from-to)377-382
Number of pages6
JournalCurrent opinion in hematology
Volume6
Issue number6
DOIs
StatePublished - Nov 8 1999

Fingerprint Dive into the research topics of 'Bone marrow transplantation for globoid cell leukodystrophy, adrenoleukodystrophy, metachromatic leukodystrophy, and Hurler syndrome'. Together they form a unique fingerprint.

Cite this