A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B

Nicole Muschol, Anja Koehn, Katharina von Cossel, Ilyas Okur, Fatih Ezgu, Paul Harmatz, Maria J. de Castro Lopez, Maria Luz Couce, Shuan Pei Lin, Spyros Batzios, Maureen Cleary, Martha Solano, Igor Nestrasil, Brian Kaufman, Adam J. Shaywitz, Stephen M. Maricich, Bernice Kuca, Joseph Kovalchin, Eric Zanelli

Research output: Contribution to journalArticlepeer-review

Fingerprint

Dive into the research topics of 'A phase I/II study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B'. Together they form a unique fingerprint.

Biochemistry, Genetics and Molecular Biology

Pharmacology, Toxicology and Pharmaceutical Science