Observing the disease course in the natural history of S

Project: Research project

Description

Observing the disease course in the natural history of Sanfilippo Syndrome Type A: A follow-up of SAN-053 participants
StatusFinished
Effective start/end date12/1/136/30/17

Funding

  • SHIRE HUMAN GENETIC THERAPIES, INC.

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Mucopolysaccharidosis III