Data Monitoring Committee: "An Open-label Ascending Dose Cohort Study to Assess the Safety,Pharmacokinetics, and Preliminary Efficacy of NeoGAA (GZ402666) in Patients with Infantile-onset PompeDisease Treated with Alglucosidase Alfa Who Demonstrate Cli

Project: Research project

Description

Data Monitoring Committee: "An Open-label Ascending Dose Cohort Study to Assess the Safety, Pharmacokinetics, and Preliminary Efficacy of NeoGAA (GZ402666) in Patients with Infantile-onset Pompe Disease Treated with Alglucosidase Alfa Who Demonstrate Cli
StatusActive
Effective start/end date2/15/1912/31/20

Funding

  • SANOFI-AVENTIS US

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Clinical Trials Data Monitoring Committees
Glycogen Storage Disease Type II
Cohort Studies
Pharmacokinetics
Safety
human GAA protein