Data Monitoring Committee: "An Open-label Ascending Dose Cohort Study to Assess the Safety, Pharmacokinetics, and Preliminary Efficacy of NeoGAA (GZ402666) in Patients with Infantile-onset Pompe Disease Treated with Alglucosidase Alfa Who Demonstrate Cli
|Effective start/end date||2/15/19 → 12/30/22|
- SANOFI-AVENTIS US
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