Project Details
Description
An Open-label Study of the Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of 12-Month Treatment with Migalastat in Pediatric Subjects (aged 12 to < 18 years) with Fabry Disease and Amenable GLA Mutations
| Status | Finished |
|---|---|
| Effective start/end date | 7/15/19 → 7/30/21 |
Funding
- AMICUS THERAPEUTICS
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