An Open-label Study of the Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of 12-Month Treatment with Migalastat in Pediatric Subjects (aged 12 to < 18 years) with Fabry Disease and Amenable GLA Mutations

Project: Research project

Project Details

Description

An Open-label Study of the Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of 12-Month Treatment with Migalastat in Pediatric Subjects (aged 12 to < 18 years) with Fabry Disease and Amenable GLA Mutations
StatusActive
Effective start/end date7/15/1912/1/20

Funding

  • Amicus Therapeutics

Fingerprint Explore the research topics touched on by this project. These labels are generated based on the underlying awards/grants. Together they form a unique fingerprint.