An Open Label Study of the Safety, Efficacy and Pharmaco

Project: Research project

Description

An Open Label Study of the Safety, Efficacy and Pharmacokinetics of Glycerol Phenylbutyrate (GPB; RAVICTI) in Pediatric Subjects under Two Years of Age with Urea Cycle Disorders (UCDs)
StatusFinished
Effective start/end date8/25/1412/31/18

Funding

  • Hyperion Therapeutics

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Inborn Urea Cycle Disorder
Pharmacokinetics
Pediatrics
Safety
glycerol phenylbutyrate