Project Details
Description
An Open-Label, Single-Arm, Multicenter Study of Intracerebral Administration of Adeno-Associated Viral Vectors Serotype rh10 Carrying the Human N-sulfoglucosamine sulfohydrolase (SGSH) cDNA for the Treatment of Mucopolysaccharidosis Type IIIA
| Status | Active |
|---|---|
| Effective start/end date | 1/25/19 → 8/31/23 |
Funding
- Lysogene
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