A Phase 2/3, multicenter, randomized, double-blinded, pl

Project: Research project

Project Details

Description

A Phase 2/3, multicenter, randomized, double-blinded, placebo-controlled, repeat???dose study to evaluate the efficacy, safety, pharmacodynamics, and pharmacokinetics of olipudase alfa in patients with acid sphingomyelinase deficiency
StatusActive
Effective start/end date2/13/172/28/22

Funding

  • GENZYME CORPORATION

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