Project Details
Description
A multi-center, randomized, active controlled clinical trial to evaluate the efficacy and safety of OTL-203 in subjects with mucopolysaccharidosis type I, Hurler syndrome (MPS-IH) compared to standard of care with allogeneic hematopoietic stem cell trans
Status | Active |
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Effective start/end date | 8/14/23 → 8/30/33 |
Funding
- ORCHARD THERAPEUTICS
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