Projects per year
Projects 2007 2020
Active
Data Monitoring Committee: "An Open-label Ascending Dose Cohort Study to Assess the Safety,Pharmacokinetics, and Preliminary Efficacy of NeoGAA (GZ402666) in Patients with Infantile-onset PompeDisease Treated with Alglucosidase Alfa Who Demonstrate Cli
2/15/19 → 12/31/20
Project: Research project
Clinical Trials Data Monitoring Committees
Glycogen Storage Disease Type II
Cohort Studies
Pharmacokinetics
Safety
Data Monitoring Committee: "A Phase 3 randomized, multicenter, multinational, double-blinded studycomparing the efficacy and safety of repeated biweekly infusions of neoGAA (GZ402666) andalglucosidase alfa in treatment-naive patients with late
2/15/19 → 12/31/20
Project: Research project
Clinical Trials Data Monitoring Committees
Safety
Therapeutics
human GAA protein
Inborn Errors Metabolism
Research