Projects per year
Personal profile
Expertise related to UN Sustainable Development Goals
In 2015, UN member states agreed to 17 global Sustainable Development Goals (SDGs) to end poverty, protect the planet and ensure prosperity for all. This person’s work contributes towards the following SDG(s):
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Collaborations and top research areas from the last five years
Projects
- 5 Active
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A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent BetaThalassemia Who Received Reni-cel
Kao, R. L. (PI)
3/27/25 → 3/26/36
Project: Research project
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MT2023-34 A Safety and Effectiveness Registry Study of Patients with B-Thalassemia Treated with Betibeglogene Autotemcel
Kao, R. L. (PI)
9/4/24 → 9/30/33
Project: Research project
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MT2022-36 A Phase 3 Study to Evaluate Efficacy and Safety of a Single Dose of Exa-cel in Subjects withSevere Sickle Cell Disease;C Genotype
Kao, R. L. (PI)
VERTEX PHARMACEUTICALS INCORPORATED
4/10/23 → 4/30/28
Project: Research project
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A Multicenter Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Dose of AutologousClustered Regularly Interspaced Short Palindromic Repeats Gene-edited CD34+ Human HematopoieticStem and Progenitor Cells (EDIT-301) in Transfusion-Depe
Kao, R. L. (PI)
8/16/22 → 8/16/27
Project: Research project
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CRE25-042: Advanced Fibrosis, TP53 Variants, and Erythroid Differentiation: Diagnostic Harbingers of ERCC6L2-Related Bone Marrow Failure Syndrome?
Valisekka, S. S., Lindstrom, M. E., Michel, O. J., Premnath, N., Eckfeldt, C. E. & Kao, R. L., Mar 28 2025, In: Journal of the National Comprehensive Cancer Network : JNCCN. 23, 35Research output: Contribution to journal › Article › peer-review
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Allogeneic Hematopoietic Cell Transplant For Bone Marrow Failure or Myelodysplastic Syndrome in Dyskeratosis Congenita/Telomere Biology Disorders: Single-Center, Single-Arm, Open-Label Trial of Reduced-Intensity Conditioning Without Radiation
Dimitrov, M., Merkle, S., Cao, Q., Tryon, R. K., Vercellotti, G. M., Holtan, S. G., Kao, R. L., Srikanthan, M., Terezakis, S. A., Tolar, J. & Ebens, C. L., Oct 2024, In: Transplantation and Cellular Therapy. 30, 10, p. 1005.e1-1005.e17Research output: Contribution to journal › Article › peer-review
1 Scopus citations -
A case of VEXAS syndrome associated with EBV-associated hemophagocytic lymphohistiocytosis
Kao, R. L., Jacobsen, A. A., Billington, C. J., Yohe, S. L., Beckman, A. K., Vercellotti, G. M. & Pearson, D. R., Mar 2022, In: Blood Cells, Molecules, and Diseases. 93, 102636.Research output: Contribution to journal › Article › peer-review
26 Scopus citations -
Hyperammonemia from Ureaplasma Infection in an Immunocompromised Child
Placone, N., Kao, R. L., Kempert, P., Ruiz, M. E., Casillas, J. N., Okada, M., Gibson, J. B., Maggi, C., O'Brien, K., Nattiv, R., Gallant, N. M. & Abrams, S. H., Mar 1 2020, In: Journal of pediatric hematology/oncology. 42, 2, p. E114-E116Research output: Contribution to journal › Article › peer-review
14 Scopus citations -
A Cetuximab-Mediated Suicide System in Chimeric Antigen Receptor-Modified Hematopoietic Stem Cells for Cancer Therapy
Kao, R. L., Truscott, L. C., Chiou, T. T., Tsai, W., Wu, A. M. & De Oliveira, S. N., Apr 2019, In: Human gene therapy. 30, 4, p. 413-428 16 p.Research output: Contribution to journal › Article › peer-review
Open Access38 Scopus citations