Projects per year
Fingerprint The Fingerprint is created by mining the titles and abstracts of the person's research outputs and projects/funding awards to create an index of weighted terms from discipline-specific thesauri.
- 19 Similar Profiles
Stem cells
Chemical Compounds
Embryonic Stem Cells
Medicine & Life Sciences
Pluripotent Stem Cells
Medicine & Life Sciences
Skeletal Muscle
Medicine & Life Sciences
Muscular Dystrophies
Medicine & Life Sciences
Muscles
Medicine & Life Sciences
Stem Cells
Medicine & Life Sciences
Muscle
Chemical Compounds
Network
Recent external collaboration on country level. Dive into details by clicking on the dots.
Projects 2008 2022
Preclinical Studies in Pluripotent Stem Cell-Derived Myogenic Progenitors to Enable a First-in-Human Phase 1 Safety/Dose Escalation Trial for Duchenne Muscular Dystrophy
Perlingeiro, R., Karachunski, P. I., McKenna, D. H., Schumacher, R. J. & Wagner, J. E.
9/15/19 → 8/31/21
Project: Research project
Pluripotent Stem Cells
Duchenne Muscular Dystrophy
Safety
Determining the therapeutic potential of pluripotent stem cell derived myogenic progenitors in the iDUX4pA mouse model
10/1/18 → 9/30/20
Project: Research project
Pluripotent Stem Cells
Therapeutics
MD160035: Scalability and Safety Studies
Perlingeiro, R., Magli, A., McKenna, D. H., Incitti, T. & Kiley, J. D.
9/30/17 → 9/29/20
Project: Research project
Safety
Therapeutics
Clinical Studies
Targeting Dystroglycanopathies using Pluripotent-derived
NIH NIAMS NATL INST OF ARTHRIT
5/10/17 → 3/31/22
Project: Research project
Gene editing of Calpain3 in LGMD2A iPS cells for the dev
COALITION TO CURE CALPAIN 3, INC.
8/1/17 → 10/31/18
Project: Research project
Cell- and Tissue-Based Therapy
Gene Editing
Limb-girdle muscular dystrophy type 2A
Research Output 1994 2019
Gene Correction of LGMD2A Patient-Specific iPSCs for the Development of Targeted Autologous Cell Therapy
Selvaraj, S., Dhoke, N. R., Kiley, J., Mateos-Aierdi, A. J., Tungtur, S., Mondragon-Gonzalez, R., Killeen, G., Oliveira, V. K. P., López de Munain, A. & Perlingeiro, R. C. R., Dec 4 2019, In : Molecular Therapy. 27, 12, p. 2147-2157 11 p.Research output: Contribution to journal › Article
Calpain
Cell- and Tissue-Based Therapy
Genes
Induced Pluripotent Stem Cells
Mutation
Pax3 cooperates with Ldb1 to direct local chromosome architecture during myogenic lineage specification
Magli, A., Baik, J., Pota, P., Cordero, C. O., Kwak, I. Y., Garry, D. J., Love, P. E., Dynlacht, B. D. & Perlingeiro, R., Dec 1 2019, In : Nature communications. 10, 1, 2316.Research output: Contribution to journal › Article
Open Access
LIM Domain Proteins
chromosomes
Chromosomes
specifications
Carrier Proteins
Pluripotent Stem Cell-Based Therapeutics for Muscular Dystrophies
Selvaraj, S., Kyba, M. & Perlingeiro, R., Sep 2019, In : Trends in Molecular Medicine. 25, 9, p. 803-816 14 p.Research output: Contribution to journal › Review article
Pluripotent Stem Cells
Muscular Dystrophies
Autologous Transplantation
Therapeutics
Technology
5
Citations
(Scopus)
Pluripotent stem cell-derived myogenic progenitors remodel their molecular signature upon in vivo engraftment
Incitti, T., Magli, A., Darabi, R., Yuan, C., Lin, K., Arpke, R. W., Azzag, K., Yamamoto, A., Stewart, R., Thomson, J. A., Kyba, M. & Perlingeiro, R. C. R., Jan 1 2019, In : Proceedings of the National Academy of Sciences of the United States of America. 116, 10, p. 4346-4351 6 p.Research output: Contribution to journal › Article
Pluripotent Stem Cells
Myoblasts
Regeneration
Gene Expression Profiling
Muscular Diseases
Screening identifies small molecules that enhance the maturation of human pluripotent stem cell-derived myotubes
Selvaraj, S., Mondragon-Gonzalez, R., Xu, B., Magli, A., Kim, H., Lainé, J., Kiley, J., McKee, H., Rinaldi, F., Aho, J., Tabti, N., Shen, W. & Perlingeiro, R. C., Nov 2019, In : eLife. 8, e47970.Research output: Contribution to journal › Article
Open Access
Pluripotent Stem Cells
Skeletal Muscle Fibers
Stem cells
Muscle
Screening