1978 …2025

Research output per year

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Fingerprint The Fingerprint is created by mining the titles and abstracts of the person's research outputs and projects/funding awards to create an index of weighted terms from discipline-specific thesauri.

  • 26 Similar Profiles

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Projects

Research Output

ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome

Ou, L., DeKelver, R. C., Rohde, M., Tom, S., Radeke, R., St. Martin, S. J., Santiago, Y., Sproul, S., Przybilla, M. J., Koniar, B. L., Podetz-Pedersen, K. M., Laoharawee, K., Cooksley, R. D., Meyer, K. E., Holmes, M. C., McIvor, R. S., Wechsler, T. & Whitley, C. B., Jan 2 2019, In : Molecular Therapy. 27, 1, p. 178-187 10 p.

Research output: Contribution to journalArticle

Open Access
  • 9 Scopus citations

    Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing

    Laoharawee, K., DeKelver, R. C., Podetz-Pedersen, K. M., Rohde, M., Sproul, S., Nguyen, H. O., Nguyen, T., St. Martin, S. J., Ou, L., Tom, S., Radeke, R., Meyer, K. E., Holmes, M. C., Whitley, C. B., Wechsler, T. & McIvor, R. S., Apr 4 2018, In : Molecular Therapy. 26, 4, p. 1127-1136 10 p.

    Research output: Contribution to journalArticle

    Open Access
  • 24 Scopus citations
    Open Access
  • 8 Scopus citations

    Lentivirus mediated correction of artemis-deficient severe combined immunodeficiency

    Punwani, D., Kawahara, M., Yu, J., Sanford, U., Roy, S., Patel, K., Carbonaro, D. A., Karlen, A. D., Khan, S., Cornetta, K., Rothe, M., Schambach, A., Kohn, D. B., Malech, H. L., McIvor, R. S., Puck, J. M. & Cowan, M. J., Jan 1 2017, In : Human gene therapy. 28, 1, p. 112-124 13 p.

    Research output: Contribution to journalArticle

    Open Access
  • 12 Scopus citations

    Prevention of neurocognitive deficiency in mucopolysaccharidosis Type II mice by central nervous system-directed, AAV9-mediated iduronate sulfatase gene transfer

    Laoharawee, K., Podetz-Pedersen, K. M., Nguyen, T. T., Evenstar, L. B., Kitto, K. F., Nan, Z., Fairbanks, C. A., Low, W. C., Kozarsky, K. F. & Mcivor, R. S., Aug 2017, In : Human gene therapy. 28, 8, p. 626-638 13 p.

    Research output: Contribution to journalArticle

  • 12 Scopus citations