1978 …2020

Research output per year

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Fingerprint The Fingerprint is created by mining the titles and abstracts of the person's research outputs and projects/funding awards to create an index of weighted terms from discipline-specific thesauri.

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Projects

Research Output

Intravenous delivery for treatment of mucopolysaccharidosis type I: A comparison of AAV serotypes 9 and rh10

Belur, L. R., Podetz-Pedersen, K. M., Tran, T. A., Mesick, J. A., Singh, N. M., Riedl, M., Vulchanova, L., Kozarsky, K. F. & McIvor, R. S., Sep 2020, In : Molecular Genetics and Metabolism Reports. 24, 100604.

Research output: Contribution to journalArticle

Open Access
  • ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome

    Ou, L., DeKelver, R. C., Rohde, M., Tom, S., Radeke, R., St. Martin, S. J., Santiago, Y., Sproul, S., Przybilla, M. J., Koniar, B. L., Podetz-Pedersen, K. M., Laoharawee, K., Cooksley, R. D., Meyer, K. E., Holmes, M. C., McIvor, R. S., Wechsler, T. & Whitley, C. B., Jan 2 2019, In : Molecular Therapy. 27, 1, p. 178-187 10 p.

    Research output: Contribution to journalArticle

    Open Access
  • 17 Scopus citations

    Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing

    Laoharawee, K., DeKelver, R. C., Podetz-Pedersen, K. M., Rohde, M., Sproul, S., Nguyen, H. O., Nguyen, T., St. Martin, S. J., Ou, L., Tom, S., Radeke, R., Meyer, K. E., Holmes, M. C., Whitley, C. B., Wechsler, T. & McIvor, R. S., Apr 4 2018, In : Molecular Therapy. 26, 4, p. 1127-1136 10 p.

    Research output: Contribution to journalArticle

    Open Access
  • 34 Scopus citations
    Open Access
  • 13 Scopus citations

    Lentivirus mediated correction of artemis-deficient severe combined immunodeficiency

    Punwani, D., Kawahara, M., Yu, J., Sanford, U., Roy, S., Patel, K., Carbonaro, D. A., Karlen, A. D., Khan, S., Cornetta, K., Rothe, M., Schambach, A., Kohn, D. B., Malech, H. L., McIvor, R. S., Puck, J. M. & Cowan, M. J., Jan 1 2017, In : Human gene therapy. 28, 1, p. 112-124 13 p.

    Research output: Contribution to journalArticle

    Open Access
  • 12 Scopus citations