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Fingerprint The Fingerprint is created by mining the titles and abstracts of the person's research outputs and projects/funding awards to create an index of weighted terms from discipline-specific thesauri.

  • 21 Similar Profiles
Beauty Medicine & Life Sciences
Tetrahydrofolate Dehydrogenase Medicine & Life Sciences
Methotrexate Medicine & Life Sciences
Genes Medicine & Life Sciences
Genetic Therapy Medicine & Life Sciences
Iduronidase Medicine & Life Sciences
Transposases Medicine & Life Sciences
Purine-Nucleoside Phosphorylase Medicine & Life Sciences

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Projects 1993 2021

Mucopolysaccharidoses
Genetic Therapy
Mucopolysaccharidoses
Beauty
B-Lymphocytes
Mucopolysaccharidoses
Hematopoietic Stem Cells
Neoplasm Genes
Therapeutics

Research Output 1978 2019

4 Citations (Scopus)

ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome

Ou, L., DeKelver, R. C., Rohde, M., Tom, S., Radeke, R., St. Martin, S. J., Santiago, Y., Sproul, S., Przybilla, M., Koniar, B. L., Podetz-Pedersen, K. M., Laoharawee, K., Cooksley, R. D., Meyer, K. E., Holmes, M. C., Mc Ivor, R. S., Wechsler, T. & Whitley, C. B., Jan 2 2019, In : Molecular Therapy. 27, 1, p. 178-187 10 p.

Research output: Contribution to journalArticle

Open Access
Mucopolysaccharidosis I
Clinical Trials
Genome
Injections
Gene Editing
18 Citations (Scopus)

Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing

Laoharawee, K., DeKelver, R. C., Podetz-Pedersen, K. M., Rohde, M., Sproul, S., Nguyen, H. O., Nguyen, T., St. Martin, S. J., Ou, L., Tom, S., Radeke, R., Meyer, K. E., Holmes, M. C., Whitley, C. B., Wechsler, T. & Mc Ivor, R. S., Apr 4 2018, In : Molecular Therapy. 26, 4, p. 1127-1136 10 p.

Research output: Contribution to journalArticle

Open Access
Mucopolysaccharidosis II
Zinc Fingers
Metabolic Diseases
Nervous System Diseases
Iduronate Sulfatase
5 Citations (Scopus)
Open Access
Iduronidase
Mucopolysaccharidoses
Dependovirus
Nervous System Diseases
Central Nervous System
12 Citations (Scopus)

Lentivirus mediated correction of artemis-deficient severe combined immunodeficiency

Punwani, D., Kawahara, M., Yu, J., Sanford, U., Roy, S., Patel, K., Carbonaro, D. A., Karlen, A. D., Khan, S., Cornetta, K., Rothe, M., Schambach, A., Kohn, D. B., Malech, H. L., McIvor, R. S., Puck, J. M. & Cowan, M. J., Jan 1 2017, In : Human gene therapy. 28, 1, p. 112-124 13 p.

Research output: Contribution to journalArticle

Open Access
Severe Combined Immunodeficiency
Lentivirus
B-Lymphocytes
Hematopoietic Stem Cells
T-Lymphocytes
12 Citations (Scopus)

Prevention of neurocognitive deficiency in mucopolysaccharidosis Type II mice by central nervous system-directed, AAV9-mediated iduronate sulfatase gene transfer

Laoharawee, K., Podetz-Pedersen, K. M., Nguyen, T. T., Evenstar, L. B., Kitto, K. F., Nan, Z., Fairbanks, C. A., Low, W. C., Kozarsky, K. F. & Mcivor, R. S., Aug 1 2017, In : Human gene therapy. 28, 8, p. 626-638 13 p.

Research output: Contribution to journalArticle

Iduronate Sulfatase
Mucopolysaccharidosis II
Central Nervous System
Genes
Glycosaminoglycans