Projects per year
Search results
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Active
A Phase I Open Label Study to Evaluate the Safety andTolerability of ISP-001 in Patients with MucopolysaccharidosisType I
12/9/21 → 1/1/26
Project: Research project
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Lysosomal Storage Disease Focused Training
Orchard, P. J. & Miller, B. S.
11/8/21 → 11/7/23
Project: Research project
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Engineered B Cells as a Universal Platform for the Treatment of Enzymopathies
Moriarity, B. S., Lund, T. C., McIvor, R. S., Orchard, P. J. & Webber, B. R.
NIH Nat'l Inst of Allergy & Infect Dis
3/1/20 → 2/28/25
Project: Research project
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Lysosomal Disease Network
Whitley, C. B., Ahmed, A., Braunlin, E. A., Cortez, D., Eisengart, J., King, K. E., Nestrasil, I. & Orchard, P. J.
NIH NAT INST OF NEURO DISORDERS & STROKE
9/15/19 → 7/31/25
Project: Research project
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Longterm Follow-up of Subjects With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product
7/1/19 → 6/30/24
Project: Research project
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A Phase 3 Study of Lenti-D Drug Product After Myeloablative Conditioning Using Busulfan and Fludarabine in Subjects ≤ 17 Years of Age With Cerebral Adrenoleukodystrophy (CALD)
Orchard, P. J., Gupta, A. O., Kenney-Jung, D. L. & Lund, T. C.
2/1/19 → 1/31/24
Project: Research project
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