Projects per year
Search results
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Active
A Phase I Open Label Study to Evaluate the Safety andTolerability of ISP-001 in Patients with MucopolysaccharidosisType I
12/9/21 → 1/1/26
Project: Research project
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Lysosomal Storage Disease Focused Training
Orchard, P. J. & Miller, B. S.
11/8/21 → 11/7/23
Project: Research project
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Engineered B Cells as a Universal Platform for the Treatment of Enzymopathies
Moriarity, B. S., Lund, T. C., McIvor, R. S., Orchard, P. J. & Webber, B. R.
NIH Nat'l Inst of Allergy & Infect Dis
3/1/20 → 2/28/25
Project: Research project
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Lysosomal Disease Network
Whitley, C. B., Ahmed, A., Braunlin, E. A., Cortez, D., Eisengart, J., King, K. E., Nestrasil, I. & Orchard, P. J.
NIH NAT INST OF NEURO DISORDERS & STROKE
9/15/19 → 7/31/25
Project: Research project
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Longterm Follow-up of Subjects With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product
7/1/19 → 6/30/24
Project: Research project
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A Phase 3 Study of Lenti-D Drug Product After Myeloablative Conditioning Using Busulfan and Fludarabine in Subjects ≤ 17 Years of Age With Cerebral Adrenoleukodystrophy (CALD)
Orchard, P. J., Gupta, A. O., Kenney-Jung, D. L. & Lund, T. C.
2/1/19 → 1/31/24
Project: Research project
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Finished
Mucopolysaccharidosis Newborn Screening meeting
Assoc of Public Health Laboratories
8/23/22 → 4/30/23
Project: Research project
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Collection of Gene Mutations for Laboratory Quality AssuranceNewborn Screening Accuracy Project
5/12/22 → 5/14/23
Project: Research project
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Safety and efficacy of Nov340 delivery of SaRNA in treating MPS I disease
Whitley, C. B., Lund, T. C., Orchard, P. J. & Ou, L.
5/1/21 → 4/29/23
Project: Research project
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National Adrenoleukodystrophy (ALD) Registry
Assoc of Public Health Laboratories
11/26/20 → 4/30/23
Project: Research project
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Data on outcomes with allogenic haematopoietic stem cell transplants in Mucopolysaccharidosis type I
Orchard, P. J., Eisengart, J., Lund, T. C. & Miller, B. S.
9/9/20 → 5/6/22
Project: Research project
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Training for the Adult Subspecialist in Inherited Metabolic Disorders
Braunlin, E. A. & Orchard, P. J.
6/17/19 → 6/17/19
Project: Research project
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Open-Label Phase 2 Pilot Study of Interferon Gamma-1b fo
Orchard, P. J. & Miller, W. P.
LUNDQUIST INSTITUTE FOR BIOMEDICAL INNO
2/1/17 → 9/30/19
Project: Research project
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Discovery of brain MRI signatures in infants with severe
Nestrasil, I., Eberly, L., Elison, J. T., Mangia, S., Michaeli, S., Mueller, B. A., Orchard, P. J. & Svatkova, A.
5/1/16 → 4/30/18
Project: Research project
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Longitudinal study of bone and endocrine disease in chil
LUNDQUIST INSTITUTE FOR BIOMEDICAL INNO
1/1/16 → 4/26/18
Project: Research project
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Characterization of the Frequency and Function of CD4+ R
Orchard, P. J. & Miller, W. P.
UNITED LEUKODYSTROPHY FOUNDATION, INC.
1/1/16 → 5/1/18
Project: Research project
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MT2013-23R: Population Pharmacokinetics of Fludarabine i
University of California San Francisco
7/1/13 → 6/30/15
Project: Research project
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Pilot Study of Administration of Intravenous Laronidase
Orchard, P. J. & Polgreen, L.
9/19/11 → 6/19/18
Project: Research project
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NHLBI Production Assistance for Cellular Therapies (PACT
Wagner, J. E., Curtsinger, J. M., Hippen, K. L., Mc Cullough, J., McKenna, D. H., Miller, J. S. & Orchard, P. J.
National Heart, Lung, and Blood Institute
1/15/10 → 1/14/15
Project: Research project
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Isoflavone-Mediated Glycosaminoglycan Reduction Therapy
Tolar, J., Charnas, L. & Orchard, P. J.
8/1/07 → 7/31/09
Project: Research project
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