Projects per year
Search results
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Active
Optimized Production and Validation of Rationally Designed AAV Vectors for Cockayne Syndrome Gene Therapy
Aslanidi, G., Kang, P. B. & Pacak, C. A.
DHHS FOOD & DRUG ADMINISTRATION (FDA)
9/1/21 → 8/31/24
Project: Research project
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Mechanisms and Treatment of Cardiac and Skeletal Muscular Dysfunction in Barth Syndrome
NATIONAL INSTITUTES OF HEALTH (NIH)
5/5/21 → 4/30/24
Project: Research project
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Finished
Development of HITI CRISPR gene therapy for dilated cardiomyopathy in a canine model
UNIVERSITY OF FLORIDA, SAREPTA THERAPEUTICS, INC.
2/1/21 → 8/31/22
Project: Research project