Projects per year
Search results
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Active
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A Phase 2, Randomized, Controlled, Multicenter Study of Vosoritide in Children With Idiopathic Short Stature (ISS)
Miller, B. S. (PI)
5/29/24 → 6/11/35
Project: Research project
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Frontiers in Congenital Disorders of Glycosylation
Sarafoglou, K. M. (PI) & Miller, B. S. (CoI)
MOUNT SINAI SCHOOL OF MEDICINE, NATIONAL INSTITUTES OF HEALTH (NIH)
4/24/24 → 7/31/25
Project: Research project
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A Study of the Genetic Determinants of Response to Growth Hormone (GH) Treatment in Children withIdiopathic Short Stature (ISS)
Miller, B. S. (PI)
1/26/24 → 2/28/34
Project: Research project
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Long-Term Follow-up of Fabry Disease Subjects who have Undergone IV Infusion with ST-920, an rAAV2/6 Human Alpha Galactosidase A Gene Therapy
Whitley, C. B. (PI), Diethelm-Okita, B. M. (CoI), Jarnes, J. R. (CoI) & Miller, B. S. (CoI)
12/4/23 → 11/30/30
Project: Research project
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A Prospective, Non-interventional (NIS), Long-Term, Post-Authorisation Safety Study (PASS) of Patients Treated with Lonapegsomatropin
Miller, B. S. (PI)
7/31/23 → 7/31/33
Project: Research project
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A Phase III study of JR-141 in Mucopolysaccharidosis type II (Hunter Syndrome) patients
Whitley, C. B. (PI) & Miller, B. S. (CoI)
11/15/22 → 11/16/25
Project: Research project
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Aeterna Zentaris DETECT: MULTICENTER, OPEN LABEL TRIAL TO INVESTIGATE THE EFFICACY AND SAFETY OF A SINGLE ORAL DOSE OF 1.0 MG/KG MACIMORELIN ACETATE AS GROWTH HORMONE STIMULATION TEST (GHST) IN PEDIATRIC PATIENTS WITH SUSPECTED GROWTH HORMONEDEFICIENCY
Miller, B. S. (PI)
4/22/21 → 4/30/26
Project: Research project
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An Open-label, Phase 1/2 Study to Evaluate the Safety and Efficacy of Single-dose PR001A in Infants with Type 2 Gaucher Disease
Whitley, C. B. (PI), Eisengart, J. (CoI), Jarnes, J. R. (CoI) & Miller, B. S. (CoI)
9/8/20 → 1/1/26
Project: Research project
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Social Buffering Over the Pubertal Transition
Gunnar, M. R. (PI), Miller, B. S. (CoI), Thomas, K. M. (CoI) & Desjardins, C. D. (Consultant/Collaborator)
NIH NAT'L INST OF CHILD HEALTH/HUMAN DEV
5/1/19 → 11/30/25
Project: Research project
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A trial comparing the effect and safety of once weekly dosing of somapacitan with daily Norditropin?? in children with growth hormone deficiency
Miller, B. S. (PI) & Sarafoglou, K. M. (Prior Principal Investigator)
4/19/19 → 4/30/25
Project: Research project