Bradley S Miller

AARDVARK THERAPEUTICS, INC

2/4/25 → 2/3/26

Project: Research project

A Phase 2, Randomized, Controlled, Multicenter Study of Vosoritide in Children With Idiopathic Short Stature (ISS)

BIOMARIN PHARMACEUTICAL, INC.

5/29/24 → 6/11/35

Project: Research project

Frontiers in Congenital Disorders of Glycosylation

Sarafoglou, K. M. (PI) & Miller, B. S. (CoI)

MOUNT SINAI SCHOOL OF MEDICINE, NATIONAL INSTITUTES OF HEALTH (NIH)

4/24/24 → 7/31/25

Project: Research project

A Study of the Genetic Determinants of Response to Growth Hormone (GH) Treatment in Children withIdiopathic Short Stature (ISS)

SANGAMO THERAPEUTICS, INC.

1/26/24 → 2/28/34

Project: Research project

Long-Term Follow-up of Fabry Disease Subjects who have Undergone IV Infusion with ST-920, an rAAV2/6 Human Alpha Galactosidase A Gene Therapy

Whitley, C. B. (PI), Diethelm-Okita, B. M. (CoI), Jarnes, J. R. (CoI) & Miller, B. S. (CoI)

12/4/23 → 11/30/30

Project: Research project

A Prospective, Non-interventional (NIS), Long-Term, Post-Authorisation Safety Study (PASS) of Patients Treated with Lonapegsomatropin

ASCENDIS PHARMA, INC

7/31/23 → 7/31/33

Project: Research project

A US Multi-center, Prospective, Non-interventional, Long-term, Effectiveness and Safety Study of Patients Treated with SKYTROFA (lonapegsomatropin) (SKYbright)

ASCENDIS PHARMA, INC

7/31/23 → 7/31/33

Project: Research project

An Open-Label, Multicenter, Phase 2 Study to Evaluate Growth and Safety of LUM-201 Following 12 Months of Daily rhGH Treatment in Children with Idiopathic Growth Hormone Deficiency who have Previously Completed the LUM-201-01 Trial

LUMOS PHARMA, INC.

5/15/23 → 6/16/28

Project: Research project

A Phase III study of JR-141 in Mucopolysaccharidosis type II (Hunter Syndrome) patients

Whitley, C. B. (PI) & Miller, B. S. (CoI)

JCR PHARMACEUTICALS

11/15/22 → 11/16/25

Project: Research project

Open-label, Single Arm, Multicenter, Phase IIIStudy on the Efficacy, Safety, and Pharmacokinetics of FP-001 42 mg ControlledRelease in Patients with Central (Gonadotropin-Dependent) Precocious Puberty

FORESEE PHARMACEUTICALS USA, INC

10/18/22 → 11/30/27

Project: Research project

Aeterna Zentaris DETECT: MULTICENTER, OPEN LABEL TRIAL TO INVESTIGATE THE EFFICACY AND SAFETY OF A SINGLE ORAL DOSE OF 1.0 MG/KG MACIMORELIN ACETATE AS GROWTH HORMONE STIMULATION TEST (GHST) IN PEDIATRIC PATIENTS WITH SUSPECTED GROWTH HORMONEDEFICIENCY

AETERNA ZENTARIS, INC.

4/22/21 → 4/30/26

Project: Research project

A Multicenter, 6-Month, Randomized, Open-Label, Active Control, ParallelArm, Phase 2b Study of Daily Oral LUM-201 in Naive-to-Treatment, Prepubertal Children with GrowthHormone Deficiency (GHD)

SANGAMO THERAPEUTICS, INC.

LUMOS PHARMA, INC.

9/9/20 → 9/30/25

Project: Research project

An Open-label, Phase 1/2 Study to Evaluate the Safety and Efficacy of Single-dose PR001A in Infants with Type 2 Gaucher Disease

Whitley, C. B. (PI), Eisengart, J. (CoI), Jarnes, J. R. (CoI) & Miller, B. S. (CoI)

PREVAIL THERAPEUTICS INC

9/8/20 → 1/1/26

Project: Research project

A Phase I/II, Multicenter, Open-Label, Single-Dose, Dose-Ranging Study to Assess the Safety and Tolerability of ST-920, a rAAV2/6 Human Alpha Galactosidase A Gene Therapy, in Subjects with Fabry Disease

Whitley, C. B. (PI) & Miller, B. S. (CoI)

2/15/20 → 10/1/26

Project: Research project

Social Buffering Over the Pubertal Transition

Gunnar, M. R. (PI), Miller, B. S. (CoI), Thomas, K. M. (CoI) & Desjardins, C. D. (Consultant/Collaborator)

NIH NAT'L INST OF CHILD HEALTH/HUMAN DEV

5/1/19 → 11/30/25

Project: Research project

A trial comparing the effect and safety of once weekly dosing of somapacitan with daily Norditropin?? in children with growth hormone deficiency

Miller, B. S. (PI) & Sarafoglou, K. M. (Prior Principal Investigator)

4/19/19 → 4/30/25

Project: Research project

Finished

A Phase 3, Randomized, Double-Blind, Dose-Ranging Evaluation of Transcutaneous Vagus Nerve Stimulation (tVNS) to Reduce Temper Outbursts in People with Prader-Willi Syndrome (PWS)

FOUNDATION FOR PRADER-WILLI RESEARCH

10/1/24 → 12/30/24

Project: Research project

A MULTICENTER LOW-INTERVENTIONAL STUDY TO EVALUATE AND MONITOR TREATMENTEXPERIENCE WITH WEEKLY GROWTH HORMONE (NGENLA) VERSUS DAILY GROWTH HORMONEINJECTIONS IN CHILDREN WITH GROWTH HORMONE DEFICIENCY

11/29/23 → 10/7/24

Project: Research project

A study comparing the effect and safety of once weekly dosing of somapacitan with daily Norditropin as well as evaluating long-term safety of somapacitan in a basket study design in children with short stature either born small for gestational age or w

5/3/22 → 8/31/23

Project: Research project

Pfizer Registry of Outcomes in Growth hormone RESearch (PROGRES): A multi-country, noninterventional prospective cohort study among patients with human growth hormone (hGH) treatments under routine clinical care

1/31/22 → 9/11/24

Project: Research project

Lysosomal Storage Disease Focused Training

Orchard, P. J. (PI) & Miller, B. S. (CoI)

SANOFI-AVENTIS US

11/8/21 → 11/7/23

Project: Research project

Assessment of Adherence and Clinical Response of Daily Growth Hormone Therapy (UMN MPR)

6/10/21 → 12/31/22

Project: Research project

Electronic Platform for Assessment of Adherence, Quality of Life, Clinical Response and Safety of Daily and Long-Acting Growth Hormone Therapy (LAuGH TRACK UMN)

MAYO CLINIC ROCHESTER, NIH NAT INST OF NEURO DISORDERS & STROKE

11/1/20 → 10/31/23

Project: Research project

Data on outcomes with allogenic haematopoietic stem cell transplants in Mucopolysaccharidosis type I

Orchard, P. J. (PI), Eisengart, J. (CoI), Lund, T. C. (CoI) & Miller, B. S. (CoI)

ORCHARD THERAPEUTICS

9/9/20 → 5/6/22

Project: Research project

Frontiers in Congenital Disorders of Glycosylation (Natural History Project)

Sarafoglou, K. M. (PI), Miller, B. S. (CoI) & Pierpont, R. (CoI)

9/15/19 → 1/31/24

Project: Research project

ATB200-03: A PHASE 3 DOUBLE-BLIND RANDOMIZED STUDY TO ASSESS THE EFFICACY AND SAFETY OFINTRAVENOUS ATB200 CO-ADMINISTERED WITH ORAL AT2221 IN ADULT SUBJECTS WITH LATE ONSETPOMPE DISEASE COMPARED WITH ALGLUCOSIDASE ALFA/PLACEBO

Whitley, C. B. (PI) & Miller, B. S. (CoI)

AMICUS THERAPEUTICS

8/1/19 → 12/31/20

Project: Research project

An Open-label Study of the Safety, Pharmacokinetics, Pharmacodynamics, and Efficacy of 12-Month Treatment with Migalastat in Pediatric Subjects (aged 12 to < 18 years) with Fabry Disease and Amenable GLA Mutations

Whitley, C. B. (PI) & Miller, B. S. (CoI)

AMICUS THERAPEUTICS

7/15/19 → 7/30/21

Project: Research project

A dose-finding trial evaluating the effect and safety of once-weekly treatment of somapacitan compared to daily Norditropin in children with short statureborn small for gestational age with no catch-up growth by 2 years of age orolder

Miller, B. S. (PI) & Sarafoglou, K. M. (Prior Principal Investigator)

4/19/19 → 4/30/24

Project: Research project

A Phase 3, Multicenter, Open-Label, Two-Part Study to Evaluate the Safety, Efficacy, Pharmacokinetics, and Pharmacodynamics of LeuprolideAcetate 45 mg 6-month formulation in Children with Central Precocious Puberty (CPP)

ABBVIE INC

11/1/18 → 9/30/23

Project: Research project

Amgen 20140444: A Phase 3 Randomized, Double-blind, Placebo-controlled, Parallel-Group Study toEvaluate the Safety and Efficacy of Denosumab in Pediatric Subjects With Glucocorticoid-inducedOsteoporosis

SANGAMO THERAPEUTICS, INC.

AMGEN INC

8/1/18 → 7/31/22

Project: Research project

A Phase I, Multicenter, Open-label, Single-dose

Whitley, C. B. (PI), Belani, K. G. (CoI), Eisengart, J. (CoI) & Miller, B. S. (CoI)

6/16/17 → 5/1/19

Project: Research project

A phase 3 randomized, multicenter, multinational, double

Whitley, C. B. (PI), Karachunski, P. I. (CoI) & Miller, B. S. (CoI)

GENZYME CORPORATION

6/14/17 → 6/29/20

Project: Research project

A Randomized, Placebo-Controlled, Blind-Start, Single-Cr

Whitley, C. B. (PI) & Miller, B. S. (CoI)

ULTRAGENYX PHARMACEUTICAL INC.

6/1/17 → 11/1/17

Project: Research project

A Phase 2/3, multicenter, randomized, double-blinded, pl

Whitley, C. B. (PI) & Miller, B. S. (CoI)

GENZYME CORPORATION

2/13/17 → 2/28/22

Project: Research project

A phase 3, open-label, randomized, multicenter, 12 month

OPKO BIOLOGICS, LTD

10/10/16 → 6/30/24

Project: Research project

A multicenter, Phase 3, randomized, open label, active-c

ULTRAGENYX PHARMACEUTICAL INC.

ASCENDIS PHARMA, INC

9/1/16 → 9/30/21

Project: Research project

A Long-Term Open-Label Treatment and Extension Study of

Whitley, C. B. (PI) & Miller, B. S. (CoI)

2/16/16 → 10/31/19

Project: Research project

A randomised, multinational, active-controlled,(open-lab

11/1/15 → 11/30/20

Project: Research project

Longitudinal Study of Skeletal Disease in Children

LUNDQUIST INSTITUTE FOR BIOMEDICAL INNO, SHIRE HUMAN GENETIC THERAPIES, INC.

10/1/15 → 9/30/20

Project: Research project

An Open-label, Single Arm, Multicenter Study on the Effi

TOLMAR, INC.

4/1/15 → 3/30/19

Project: Research project

Comparison of VRS-317, a Long-acting Human Growth Hormon

VERSARTIS, INC

3/16/15 → 12/31/17

Project: Research project

A PHASE IV, MULTICENTER, OPEN-LABEL STUDY OF THE IMMUNOG

GENENTECH, INC.

1/1/15 → 12/31/18

Project: Research project

Retrospective Hypophosphatasia (HPP) EMR Analysis

ALEXION PHARMACEUTICALS

1/1/15 → 11/3/20

Project: Research project

ANSWER Program Registry American Norditropin Studies:

Miller, B. S. (PI), Bellin, M. D. (CoI), Nathan, B. M. (CoI), Petryk, A. (CoI), Polgreen, L. (CoI) & Sarafoglou, K. M. (CoI)

9/2/14 → 9/2/17

Project: Research project

An Open-Label, Long-Term Extension Study of the Safety

VERSARTIS, INC

12/19/13 → 12/31/22

Project: Research project

A Multicenter, Observational Registry of Pediatric Femal

ENDO PHARMACEUTICALS INC

8/1/13 → 7/31/18

Project: Research project

Post-approval Safety Study to Monitor the Long-term Safe

OPTUMINSIGHT LIFE SCIENCES, INC.

12/1/12 → 11/30/19

Project: Research project

A long-acting human growth hormone (VRS-317) in pre-pube

VERSARTIS, INC

8/13/12 → 9/30/14

Project: Research project

An open-label, non-comparative, multicenter study on the

SYNEOS HEALTH, INC

6/1/12 → 2/13/14

Project: Research project

A Post-Marketing, Multicenter, Two-Arm Registry Study of