Projects per year
Search results
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Customer Discovery and Business Analysis for Arteriopulse
Durfee, W. (PI) & Broomhead, J. R. (CoI)
THE NATIONAL SCIENCE FOUNDATION
1/14/25 → 4/13/25
Project: Research project
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Discovery and validation of single cell biomarkers for clinical outcome in sickle cell disease
Wood, D. K. (PI), Datta, Y. H. (CoI), Gupta, A. O. (CoI) & Vercellotti, G. M. (CoI)
NIH NAT'L HEART, LUNG, AND BLOOD INSTITU
12/15/24 → 11/30/25
Project: Research project
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GenoKrabbe: A Comprehensive Genotype-Phenotype Database for Krabbe Disease
Orchard, P. J. (PI), Gupta, A. O. (CoI), Pillai, N. (CoI), Braun, J. A. (Other Role) & Shanley, R. M. (Other Role)
ROSENAU FAMILY RESEARCH FOUNDATION
11/1/24 → 10/31/27
Project: Research project
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Characterization and In Vivo Gene Therapy Using a Novel Fanconi Anemia Mouse Model of Bone Marrow Failure
Moriarity, B. S. (PI), Wagner, J. E. (CoI) & Webber, B. R. (CoI)
11/1/24 → 10/31/27
Project: Research project
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Engineered Gamma Delta T cells for Systemic Correction of Dystrophic Epidermolysis Bullosa
Moriarity, B. S. (PI), Ebens, C. (CoI) & Webber, B. R. (Co-Principal Investigator)
KOMMODO THERAPEUTICS LLC, NIH NIAMS NATL INST OF ARTHRIT
8/22/24 → 7/31/25
Project: Research project
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BMT Core - University of Minnesota
Juckett, M. B. (PI), Ebens, C. (Co-Principal Investigator), Merino, A. M. (Other Role) & Miller, J. S. (Other Role)
NIH NAT'L HEART, LUNG, AND BLOOD INSTITU
8/15/24 → 6/30/31
Project: Research project
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Immune Cell therapy for RDEB
Tolar, J. (PI) & Osborn, M. J. (CoI)
7/22/24 → 7/21/25
Project: Research project
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Wastewater Surveillance Testing
Osborn, M. J. (PI) & Doss, C. R. (CoI)
MN DEPARTMENT OF HEALTH, U.S. DEPARTMENT OF HEALTH & HUMAN SVCS
4/8/24 → 7/31/25
Project: Research project
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Phase 1 Clinical Trial of Myogenic Progenitors for DMD
Kang, P. B. (PI), Cheng, E. Y. (CoI), Karachunski, P. I. (CoI), McKenna, D. H. (CoI), Perlingeiro, R. (CoI) & Wagner, J. E. (CoI)
3/4/24 → 3/3/27
Project: Research project
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Cancer Center Support Grant
Yee, D. (PI), Antonarakis, E. (CoI), Beckman, K. B. (CoI), Betts, B. (CoI), Blaes, A. H. (CoI), Eaton, A. (CoI), Ellis, K. M. (CoI), Felices, M. (CoI), Geller, M. A. (CoI), Ghebre, R. G. (CoI), Griffin, T. J. (CoI), Hallstrom, T. C. (CoI), Harki, D. A. (CoI), Hatsukami, D. K. (CoI), Hirsch, B. A. (CoI), Huang, R. S. S. (CoI), Johnson, S. (CoI), Juckett, M. B. (CoI), Lange, C. A. (CoI), Le, C. T. (CoI), Luo, X. (CoI), McKenna, D. H. (CoI), Miller, J. S. (CoI), Moriarity, B. S. (CoI), Muretta, J. M. (CoI), Murray, T. (CoI), Nelson, H. H. (CoI), Ondrey, F. G. (CoI), Patel, M. R. (CoI), Pennell, C. A. (CoI), Petersen, A. J. (CoI), Peterson, L. A. (CoI), Poynter, J. (CoI), Pratt, R. J. (CoI), Sarver, A. L. (CoI), Schendzielos, D. L. (CoI), Schilz, A. (CoI), Schwertfeger, K. (CoI), Seelig, D. (CoI), Shimizu, Y. (CoI), Stepanov, I. (CoI), Temiz, N. A. (CoI), Ventz, S. (CoI), Villalta, P. W. (CoI), Vogel, R. (CoI), Wagner, J. E. (CoI), Wang, J. (CoI), Webber, B. R. (CoI), Weigel, B. J. (CoI), Yamamoto, M. (CoI) & Zhang, L. (CoI)
NIH NATIONAL CANCER INSTITUTE (NCI)
2/1/24 → 1/31/29
Project: Research project
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Transforming treatment of inherited bone marrow failure in Fanconi anemia by in vivo precise genome editing
Moriarity, B. S. (PI), Wagner, J. E. (CoI) & Webber, B. R. (CoI)
2/1/24 → 1/31/26
Project: Research project
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Base Editing and Prime Editing for HIV/SCD Cures
Osborn, M. J. (PI)
THE BROAD INSTITUTE, INC., BILL & MELINDA GATES FOUNDATION
10/1/23 → 9/30/26
Project: Research project
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Development of an Off the Shelf Erythrocyte-Based Resuscitation Fluid for Hemostasis and Improved Oxygen Delivery
Osborn, M. J. (PI)
THE HENRY M. JACKSON FOUNDATION, U.S. DEPARTMENT OF DEFENSE
9/30/23 → 9/29/27
Project: Research project
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Human Organ-on-Chip Platforms for Assessment and Development of Countermeasures for Radiation Exposure
Panoskaltsis-Mortari, A. (PI), Azarin, S. M. (CoI), Bigliardi Qi, M. (CoI) & Ogle, B. M. (CoI)
THE GENEVA FOUNDATION, UNIFORMED SVC UNIV OF THE HEALTH SCI
9/25/23 → 9/24/27
Project: Research project
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P300/CBP inactivation, a novel epigenetic therapeutical approach for Ewing sarcomas
Bosnakovski, D. (PI), Das, S. (CoI) & Mills, L. J. (CoI)
9/1/23 → 8/31/25
Project: Research project
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Analysis of long-term somatic and functional outcomes of hematopoietic cell transplantation (HCT) for alpha-mannosidosis, with consideration of prospects for gene therapy
Eisengart, J. (PI), Lund, T. C. (CoI) & Yund, B. D. (CoI)
INTL SOCIETY FOR MANNOSIDOSIS & RELATED
9/1/23 → 8/31/25
Project: Research project
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A multi-center, randomized, active controlled clinical trial to evaluate the efficacy and safety of OTL-203 in subjects with mucopolysaccharidosis type I, Hurler syndrome (MPS-IH) compared to standard of care with allogeneic hematopoietic stem cell trans
Gupta, A. O. (PI)
8/14/23 → 8/30/33
Project: Research project
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HMGB1 in EB-Associated Squamous Cell Carcinoma
Bui, K. G. (PI)
NIH NATIONAL CANCER INSTITUTE (NCI)
8/1/23 → 7/31/27
Project: Research project
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Collection of Gene Mutations for Laboratory Quality Assurance: Newborn Screening Accuracy Project
Gupta, A. O. (PI) & Pillai, N. (CoI)
SEQUOIA FOUNDATION, CENTERS FOR DISEASE CONTROL & PREVENTION
5/15/23 → 5/14/28
Project: Research project
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Off-the-Shelf Immune Effector Cells for Hematological Malignancies
Wagner, J. E. (PI), Bachanova, V. (CoI), Betts, B. (CoI), Brunstein, C. G. (CoI), Cichocki, F. M. (CoI), De For, T. E. (CoI), Eaton, A. (CoI), Hippen, K. L. (CoI), Luo, X. (CoI), Maakaron, J. (CoI), McKenna, D. H. (CoI) & Tolar, J. (CoI)
NIH NATIONAL CANCER INSTITUTE (NCI)
5/5/23 → 4/30/28
Project: Research project
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A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects with Cerebral Adrenoleukodystrophy
Lund, T. C. (PI)
3/23/23 → 3/31/28
Project: Research project
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Project 2: Novel Approaches to Inducing Lung Allograft Tolerance in NHPs
Blazar, B. R. (PI) & Hippen, K. L. (CoI)
MASSACHUSETTS GENERAL HOSPITAL, NIH Nat'l Inst of Allergy & Infect Dis
3/23/23 → 2/29/28
Project: Research project
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A PrOspective Registry of Pediatric Cellular Therapy Patients at risk for Endothelial Dysfunction,Sinusoidal Obstruction Syndrome and/or Multi-Organ Dysfunction Syndrome (MODS).
Ebens, C. (PI)
UNIV. OF TX M.D. ANDERSON CANCER CENTER, JAZZ PHARMACEUTICALS, INC.
10/25/22 → 12/31/26
Project: Research project
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REVEAL - Research Evaluating Vagal Excitation and Anatomical Linkages.
Osborn, J. (PI), Crawford, P. (CoI), Darrow, D. (CoI), Drawz, P. E. (CoI), Dudley, S. (CoI), Eberly, L. (CoI), Fonkoue, I.-A. T. (CoI), Henry, T. R. (CoI), Hering, B. J. (CoI), Ikramuddin, S. (CoI), Johnson, M. D. (CoI), Keller-Ross, M. L. (CoI), Lim, K. O. (CoI), Lim, H. H. (CoI), Loavenbruck, A. J. (CoI), McCarty, C. A. (CoI), Meyer, M. (CoI), Mueller, B. A. (CoI), Murray, T. (CoI), Nahas, Z. (CoI), Netoff, T. I. (CoI), Panoskaltsis-Mortari, A. (CoI), Park, M. C. (CoI), Puchalska, P. (CoI), Ramachandran, S. (CoI), Singh, A. (CoI), Talkachova, A. (CoI), Tignanelli, C. J. (CoI) & Walczak, T. S. (CoI)
NATIONAL INSTITUTES OF HEALTH (NIH)
9/23/22 → 8/31/25
Project: Research project
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To explore the molecular and cellular effects of transient DUX4 expression in skeletal muscle
Bosnakovski, D. (PI), Gearhart, M. D. (CoI) & Magli, A. (CoI)
NIH NIAMS NATL INST OF ARTHRIT
9/1/22 → 6/30/27
Project: Research project
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In Vivo Prevention of Murine GVHD
Blazar, B. R. (PI) & Panoskaltsis-Mortari, A. (CoI)
NIH Nat'l Inst of Allergy & Infect Dis
7/1/22 → 6/30/27
Project: Research project
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Enhancing Treg Therapeutic Efficacy in GVHD
Blazar, B. R. (PI), Griffin, T. J. (CoI), Hippen, K. L. (CoI) & Osborn, M. J. (CoI)
NIH NAT'L HEART, LUNG, AND BLOOD INSTITU
5/15/22 → 3/31/26
Project: Research project
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A Phase I Open Label Study to Evaluate the Safety andTolerability of ISP-001 in Patients with MucopolysaccharidosisType I
Orchard, P. J. (PI)
12/9/21 → 1/1/26
Project: Research project
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Phase 3, Randomized, Double-Blind, Placebo-Controlled Trial, with Cross-Over, of Posoleucel (ALVR105) for the Treatment of Adenovirus Infection in Pediatric and Adult Participants Receiving Standard of Care Following Allogeneic Hematopoietic Cell Transpl
Orchard, P. J. (PI)
10/25/21 → 10/31/26
Project: Research project
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Sensory Function and Chronic Pain in Cerebral Palsy
Symons, F. J. (PI), Erickson, D. J. (CoI), Panoskaltsis-Mortari, A. (CoI), Simone, D. A. (CoI), Walk, D. (CoI) & Wilcox, G. L. (CoI)
NIH NAT'L INST OF CHILD HEALTH/HUMAN DEV
5/14/21 → 2/28/27
Project: Research project
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A Phase 3, Open-label, Single Arm, Multicenter Study of Ravulizumab in Addition to Best Supportive Care in Pediatric Participants (from 1 month to < 18 years of age) with Thrombotic Microangiopathy (TMA) after Hematopoietic Stem Cell Transplantation (HSC
Srikanthan, M. (PI) & Smith, A. R. (Prior Principal Investigator)
9/20/20 → 8/31/25
Project: Research project
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Skin-targeted Cell Therapy for Recessive Dystrophic Epidermolysis Bullosa
Tolar, J. (PI), Moriarity, B. S. (CoI), Osborn, M. J. (CoI) & Webber, B. R. (CoI)
NIH NIAMS NATL INST OF ARTHRIT
9/1/20 → 8/31/25
Project: Research project
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Probing the activity of DUX4 in FSHD
Kyba, M. (PI)
NIH NIAMS NATL INST OF ARTHRIT
8/18/20 → 7/31/25
Project: Research project
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Evaluation of the Oral and Lung Microbiota and Inflammation in Chronic Obstructive Pulmonary DiseaseFrequent Exacerbators
U.S. DEPARTMENT OF VETERANS AFFAIRS
6/1/20 → 5/31/25
Project: Research project
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Development and Psychometric Testing of a Pediatric Chronic Graft-Versus-Host Disease (GVHD) Symptom Scale (PCSS)
MacMillan, M. L. (PI)
WESTAT, INC., NATIONAL INSTITUTES OF HEALTH (NIH)
5/1/20 → 4/30/25
Project: Research project
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A Phase I Study to Evaluate The Safety and Tolerability of Tandemly-Purified Allogeneic CD34+CD90+ HSC Administered Following Conditioning with AMG 191 to Achieve Engraftment and Immune Reconstitution in Patients with SCID
Ebens, C. (PI) & Smith, A. R. (Prior Principal Investigator)
5/1/20 → 4/30/25
Project: Research project
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An Open Label Expanded Access Study of Omidubicel, for Allogeneic Transplantation in Patients with Hematological Malignancies
Wagner, J. E. (PI) & Brunstein, C. G. (Prior Principal Investigator)
4/23/20 → 4/30/25
Project: Research project
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Lysosomal Disease Network
Whitley, C. B. (PI), Ahmed, A. (CoI), Braunlin, E. A. (CoI), Cortez, D. (CoI), Eisengart, J. (CoI), King, K. E. (CoI), Nestrasil, I. (CoI) & Orchard, P. J. (CoI)
NIH NAT INST OF NEURO DISORDERS & STROKE
9/15/19 → 7/31/25
Project: Research project
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A Phase 3 Study Evaluating Gene Therapy by Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo with the LentiGlobin BB305 Lentiviral Vector in Subjects with Sickle Cell Disease.
Gupta, A. O. (PI) & Smith, A. R. (Prior Principal Investigator)
9/1/19 → 7/31/28
Project: Research project
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Training in Lung Science
Wendt, C. H. (PI), Bitterman, P. B. (CoI), Ingbar, D. H. (CoI) & Panoskaltsis-Mortari, A. (CoI)
NIH NAT'L HEART, LUNG, AND BLOOD INSTITU
8/1/19 → 7/31/25
Project: Research project